Efzimfotase alfa demonstrated improvements in bone health in treatment-naïve pediatric patients with hypophosphatasia achieving median difference of 1.67 vs placebo in RGI-C Score at week 25 in MULBERRY Phase III trial
Improved Assessment of Health Care Worker Attitudes about Prenatal Alcohol Exposure and Fetal Alcohol Spectrum Disorders May Improve Prevention and Treatment
World Birth Defects Day: “Behind every diagnosis is a story that deserves to be supported through strong public policies and strengthened health systems”